Buscar resultados de ensayos clínicos
DNA Repair-Deficiency Disorders - 25 Studies Found
Estado | Estudiar |
Active, not recruiting |
Nombre del estudio: Autologous Transplant of EFS-ADA Modified Bone Marrow Cells for ADA-Deficient Severe Combined Immunodeficiency (SCID) Condición: ADA-SCID Fecha: 2013-05-07 Intervenciones: Genetic: EFS-ADA transduced CD34+ cells from the bone marrow Eligible subjects will undergo bone marrow |
Terminated |
Nombre del estudio: Hematopoietic Stem Cell Transplantation (HSCT) for Children With SCID Utilizing Alemtuzumab, Plerixafor & Filgrastim Condición: Severe Combined Immunodeficiency Fecha: 2010-08-09 Intervenciones:
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Terminated |
Nombre del estudio: rAd-p53 Gene Therapy for Advanced Oral and Maxillofacial Malignant Tumors Condición: Advanced Oral and Maxillofacial Malignant Tumors Fecha: 2009-05-11 Intervenciones:
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Completed |
Nombre del estudio: MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID Condición: Severe Combined Immunodeficiency Fecha: 2008-11-19 Intervenciones: Biological: ADA gene transfer Autologous CD34+ cells transduced with the retroviral vector MND-ADA, carr |
Completed |
Nombre del estudio: Gene Therapy for ADA-SCID Condición: Severe Combined Immunodeficiency Syndrome Fecha: 2008-01-08 Intervenciones: Genetic: gene transduced PBL and/or gene transduced HSC infusions of autologous PBL and/or HSC transduce |
Completed |
Nombre del estudio: Transplantation of Hematopoietic Cells in Children With Severe Combined Immunodeficiency Syndrome Condición: Severe Combined Immunodeficiency Fecha: 2005-09-07 Intervenciones:
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Recruiting |
Nombre del estudio: Genetic Basis of Immunodeficiency Condición: Severe Combined Immunodeficiency Fecha: 2003-02-20 |
Completed |
Nombre del estudio: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency Condición: Severe Combined Immunodeficiency Syndrome Fecha: 2001-06-27 Intervenciones: Drug: CD34+ cells transduced with ADA retrovir |
Completed |
Nombre del estudio: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study Condición: Severe Combined Immunodeficiency Fecha: 1999-11-03 Intervenciones:
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Completed |
Nombre del estudio: Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia Condición: Fanconi Anemia Fecha: 2009-08-24 Intervenciones: Drug: Etanercept All qualified subjects receive 24 weekly subcutaneous injections of Etanercept. |